mRNA therapies in liver Inherited Metabolic Diseases

About this episode

This episode discusses the potential of mRNA therapy for treating liver inherited metabolic diseases with insights from experts in the field.

mRNA therapy is emerging as a serious therapeutic platform for liver inherited metabolic diseases. In this episode, James Nurse speaks with Sonam Gurung and Julien Baruteau about their JIMD paper exploring how mRNA can be used for protein replacement, how lipid nanoparticles help target the liver, and where this approach may complement gene therapy, transplantation and standard care. A clear look at a rapidly evolving field. Delivering the Message: Translating mRNA Therapy for Liver Inherited Metabolic Diseases Sonam Gurung, et al https://doi.org/10.1002/jimd.70078

People in this episode

Host: James Nurse

Guests: Sonam Gurung, Julien Baruteau

Topics covered

• mRNA therapy
• liver diseases
• protein replacement
• lipid nanoparticles
• gene therapy
• transplantation
• standard care

Keywords

• mRNA therapy
• liver diseases
• protein replacement
• lipid nanoparticles
• gene therapy
• transplantation
• metabolic diseases

Mentioned in this episode

Organizations: Journal of Inherited Metabolic Disease

Books & works: Delivering the Message: Translating mRNA Therapy for Liver Inherited Metabolic Diseases

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